Collaborative Project #10: Toward Safer Gene Therapy for Hemophilia A
Collaborating Investigator: Roland Herzog, PhD Affiliation: Riley Children’s Foundation Professor of Immunology, Indiana University Funding Source: NIH Funding: Number: P01HL160472 Project Period: 02/05/22-01/31/27 Significance The X-linked bleeding disorder Hemophilia A is caused by a deficiency in the clotting protein factor VIII (FVIII), and FVIII gene therapy thus provides a promising strategy for disease treatment....